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Novartis gene therapy for SMA to be cost effective up to $900000: US group


Novartis gene therapy for SMA to be cost effective up to $900000: US group
Novartis has said the price will be determined in negotiations with health plans, but it believes the gene therapy would be cost-effective at $4 million to $5 million as a one-time treatment.
 
U.S: An experimental gene therapy for spinal muscular atrophy (SMA) developed by Novartis AG would be worth up to $900,000, according to an independent U.S. nonprofit organization that reviews the value of drugs and medical treatments.

The Boston-based Institute for Clinical and Economic Review (ICER) made the determination using a commonly cited cost-effectiveness threshold that values each “quality-adjusted life year” (QALY) gained at $100,000 to $150,000.

Read Also: Novartis India Q3 net profit dips 31 per cent to Rs 12.87 crore

If each QALY gained were assessed at $500,000, ICER found the gene therapy, Zolgensma, would be cost effective at just over $5 million.

Novartis has said the price will be determined in negotiations with health plans, but it believes the gene therapy would be cost-effective at $4 million to $5 million as a one-time treatment.

Read Also: Novartis Aimovig not cost effective: UK price watchdog

The company said in an emailed statement on Friday that “both the rare disease community and various governmental bodies” suggest that $500,000 per QALY “is the appropriate standard to protect vulnerable populations and allow access to innovative, transformational therapies.”

SMA can lead to paralysis, breathing difficulty and death. It is the leading genetic cause of death in infants.

Read Also: Novartis to buy France’s CellforCure to boost cell, gene therapy

Gene therapies use engineered viruses to carry healthy genetic material into a person’s cells to replace faulty or mutated genes that cause a disease or condition.



Source: Reuters
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